id author title date pages extension mime words sentence flesch summary cache txt js956d59x83 Eve A. Granatosky Biosynthetic Access to the GEX1A Scaffold: A Novel Therapeutic Approach for Niemann-Pick Type C Disease 1904 .txt text/plain 351 13 30 We finally examined the effects of GEX1A on in vitro models of NPC disease at the cellular and molecular levels. A complete analysis of this expression data, which includes isoform-specific information relevant to GEX1A's role in splicing modulation, is underway, and will be a valuable contribution to understanding how this natural product, and potentially other structurally related scaffolds, has a beneficial therapeutic effect in the context of NPC disease. cache/js956d59x83.txt txt/js956d59x83.txt